Annual Gene Therapy Symposium for
Heart, Lung, and Blood Diseases
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Past Symposia:

UC Davis


4th Annual Gene Therapy Symposium for Heart, Lung, and Blood Diseases
Focus Topic: Translational Research
November 16-18, 2005 - Sonoma, California



Wednesday, November 16, 2005 - Welcoming Reception


Thursday, November 17, 2005

Keynote Speaker
• Katherine A. High, M.D. (Children's Hospital of Philadelphia)
"Clinical Gene Transfer Studies for Hemophilia B"

Session I
• Bruce Levine, Ph.D. (University of Pennsylvania)
"Translating Gene Transduced Activated T Cells From Research to Clinical Trials"
• R. Jude Samulski , Ph.D. (University of North Carolina at Chapel Hill)
"Synthetic Biological Nano-Particles, the Next Generation of Gene Delivery Systems"
• Ian MacLachlan , Ph.D. (Protiva Biotherapeutics, Inc.)
"Considerations for the Development of Nucleic Acid-Based Drugs"

Student/Fellow Presentations and Poster Session
- Link to Information

Session II
• John F. Engelhardt, Ph.D. (University of Iowa)
"Species Choice for Animal Modeling Cystic Fibrosis and Gene Therapy to the Airway"
• Katherine P. Ponder, M.D. (Washington University)
"Immune Responses After Neoatal Gene Therapy in Cats Can Limit Gene Therapy but Can be Blocked With CTLA4-Ig"
• Mary E. Fabry, Ph.D. (Albert Einstein College of Medicine)
"Use of Thalassemic and Sickle Transgenic Mouse Models to Evaluate Protocols for Gene Therapy and Arginine Supplementation"

Practical Strategies:
Center for Fetal Monkey Gene Transfer for Heart, Lung, and Blood Diseases
• Alice F. Tarantal, Ph.D. (University of California, Davis)
• Barry J. Byrne, M.D., Ph.D. (University of Florida)
"Sustained Correction of Pompe Disease Using AAV Vectors: Effects of Early Gene Transfer on Cardiac and Pulmonary Function"
• Mark A. Kay, M.D., Ph.D. (Stanford University)
"RNAi Based Approaches for Viral Hepatitis "
• Mervin C. Yoder, M.D. (Indiana University)
"Identification of Endothelial Colony Forming Cells in Fetal Rhesus Peripheral Blood"

Dinner Speaker:
• Barry Byrne, M.D., Ph.D.
Niebaum-Coppola Winery, St. Helena, California


Friday, November 18, 2005

Workshop: Updates from the NHLBI
• Sonia I. Skarlatos, Ph.D. (NHLBI, NIH)

Session III
• Harald Ott, M.D. (University of Minnesota) "Cells, Gene and Matrix: What's the Next Magic for Cardiovascular Repair?"
• Duncan J. Stewart, M.D., FRCPC (University of Toronto)
"Vascular Regeneration: A Novel Treatment for Pulmonary Arterial Hypertension?"


Student/Fellow Presentations and Poster Session - Link to Information

Session IV
• Hans-Peter Kiem, M.D. (Fred Hutchinson Cancer Research Center)
"Hematopoietic Stem Cell Gene Transfer and Expansion in Nonhuman Primates "
• Jan A. Nolta, Ph.D. (Washington University in St. Louis)
"Immune Deficient Mouse Models to Study Human Mesenchymal and Hematopoietic Stem Cell Engraftment and Tissue Repair: Working Toward Cellular Therapies "



  Supported by the National Heart, Lung, and Blood Institute with additional support provided by the National Institute of Allergy and Infectious Diseases, National Institute of Biomedical Imaging and Bioengineering, National Center for Research Resources, National Institutes of Health, and the California National Primate Research Center, University of California, Davis, and Stem Cell Technologies, Inc.