7th Annual Gene Therapy Symposium for Heart, Lung, and Blood Diseases
Focus Topic: Preclinical Studies
November 19-21, 2008 - Sonoma, California

Program

Wednesday, November 19, 2008 - Welcoming Reception

Thursday, November 19, 2008

Keynote Speaker

• Barry J. Byrne,, M.D. Ph.D. (University of Florida)
  “Pathways to Clinical Studies in Gene Therapy: The Critical Role of Preclinical Models in Molecular Medicine”

Session I  

• Kenneth G. Cornetta, M.D. (Indiana University)
  “The Challenges of Generating Clinical Grade Lentiviral Production”

• James M. Wilson, M.D., Ph.D. (University of Pennsylvania)
  “Viral Infections, Vaccines, and Gene Therapy”

• Nancy Smyth Templeton, Ph.D. (Baylor College of Medicine)
  “Optimization of Non-Viral Vectors for Preclinical Studies”

Session II   

• Roger J. Hajjar, M.D. (Mount Sinai School of Medicine)
  “Clinical Gene Therapy for Heart Failure”
  
  
• Joseph C. Wu, MD, Ph.D. (Stanford University)
  “Molecular Imaging of Cardiac Gene Therapy”

• Mervin C. Yoder, M.D. (Indiana University)
  “New Insights into Methods to Identify Circulating Endothelial Cells and Hematopoietic Progenitor Cells that Represent the Circulating Cells Involved in Cardiovascular Disease”

“Practical Strategies”: Tissue Engineering and the Challenges of Translating to Human Applications

• Gordana V. Vunjak-Novakovic Ph.D. (Columbia University)

Friday, November 21, 2008

Workshop: “Preclinical Consideration for Gene Therapy Products: CBER Perspective”

• Mercedes Serabian, M.S., D.A.B.T.
  (FDA, CBER, OCTGT)

Session III

• Hanna K.A. Mikkola, M.D., Ph.D. (University of California, Los Angeles)
  “Defining and Recreating the Human Fetal Hematopoietic Stem Cell Microenvironment”

• Connie J. Eaves, Ph.D. (Terry Fox Laboratory)
  “Hematopoietic Stem Cells and Their Regulation - The Devil in the Details”
  
  
• Donald B. Kohn, M.D. (Chldrens Hospital Los Angeles)
  "Gene Therapy Using Hematopoietic Stem Cells"

Session IV

• Bernard Thébaud, M.D., Ph.D. (University of Alberta)
  “Role of Angiogenesis During Lung Development, Injury, and Repair”
  
  
• Joseph Zabner, M.D. (University of Iowa)
  “Generation of Novel AAV Vectors for Cystic Fibrosis Gene Therapy”