Annual Gene Therapy Symposium for
Heart, Lung, and Blood Diseases
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UC Davis


9th Annual Gene Therapy Symposium for Heart, Lung, and Blood Diseases
Focus Topic: Gene Expression
November 17-19, 2010 - Sonoma, California



Wednesday, November 17, 2010 - Welcoming Reception


Andrew M. Scharenberg, M.D.Thursday, November 18, 2010

Keynote Speaker

  • Andrew M. Scharenberg, M.D. (University of Washington)
    “Strategies for Enhancing Site Specific Genome Engineering Efficiency”

Session I  

  • Brian D. Brown, Ph.D. (Mt Sinai Medical Center)
    “Utilizing Synthetic microRNA Sites for Targeting Vector Expression”
  • David V. Schaffer, Ph.D. (University of California, Berkeley)
    “Directed Evolution of New Viruses with Novel Gene Delivery Properties”
  • Michele P. Calos, Ph.D. (Stanford University)
    “Triple Recombinase Strategy to Make and Modify Induced Pluripotent Stem Cells”
Student/Fellow Presentations and Poster Session - Link to Information

Session II   

  • W. Robb MacLellan, M.D. (UC Los Angeles)
    “Human Cardiovascular Progenitor Cells, Induced Pluripotent Stem Cells and Epigenetic Regulation of Cardiac Fate”
Beverly L. Davidson, Ph.D.
  • Ian McNiece, Ph.D. (University of Miami)
    “Mesenchymal Stem Cells and Ischemic Heart Repair”
  • Ian MacLachlan, Ph.D. (Tekmira Pharmaceuticals)
    “Integrating Preclinical and Clinical Experience in the Development of the Next Generation of siRNA Products”

“Practical Strategies”: Evaluating the Safety of RNAi-based Therapeutics

  • Beverly L. Davidson, Ph.D. (University of Iowa)

Jacuzzi Family Vineyards

John C. Gore, Ph.D.

Friday, November 19, 2010

Workshop: “Biomaterials and Tissue Engineering”

  • Lonnie D. Shea, Ph.D. (Northwestern University)

Session III

  • Mark A. Krasnow, M.D., Ph.D. (Stanford University)
    “Progenitor and Stem Cells in Lung Development and Disease”
  • Angela Panoskaltsis-Mortari, Ph.D. (University of Minnesota)
    “Bioengineering of the Lung using iPS Cells and Decellularized Lung Matrix”

  • Barry J. Byrne, M.D., Ph.D. (University of Florida)
    "Phase 2 Trial of rAAV1-hAAT"
Student/Fellow Presentations and Poster Session - Link to Information

Session IV

  • R. Keith Humphries, M.D., Ph.D. (University of British Columbia)
    “Targeting the Untargetable: Leukemogenic Transcription Factors”

  • Mary C. Dinauer, M.D., Ph.D. (Washington University)
    “Antibody Targeting c-Kit as a Pre-Transplant Conditioning for Gene Therapy”

  • Eirini P. Papapetrou, M.D., Ph.D. (Memorial Sloan Kettering)
    “Genetic Engineering of Patient-Specific Induced Pluripotent Stem Cells in Genomic 'Safe Harbors'”


Supported by the National Heart, Lung, and Blood Institute, National Institutes of Health. Additional support provided by the National Institute of Allergy and Infectious Diseases (NIAID), National Institute of Biomedical Imaging and Bioengineering (NIBIB); NIH; California Institute for Regenerative Medicine (CIRM); California National Primate Research Center and Office of Research, UC Davis; and the UC Davis Clinical and Translational Science Center.